Phase II trials
Who sets the design
Active comparator / placebo
Phases
Accelerated approval pathways
- Conditional marketing authorisation (EMA)
- Accelerated assessment (EMA)
Adaptive clinical trial designs
Smaller and more flexible clinical trials
- Phase I/II
- Phase II/III
Surrogate endpoints, biomarkers vs survival
RWE, registries
Patient involvement
Compassionate use
Documentation and submission modifications
Post market requirements